Clinical trial shows newborns with spinal muscular atrophy can start treatment at birth

Spinal muscular atrophy (SMA) is a rare genetic condition that causes progressive muscle weakness, which, when untreated, prevents infants with the most severe form from gaining motor development—never gaining the ability to sit—and typically leads to death before 2 years of age.

This article was originally published on MedicalXpress.com

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