Nanoparticle-based gene editing could expand treatment options for cystic fibrosis

UCLA researchers have developed a lipid nanoparticle-based gene-editing approach capable of inserting an entire healthy gene into human airway cells, restoring key biological function in a laboratory model of cystic fibrosis and establishing a potential new path toward mutation-agnostic gene therapy for inherited lung diseases.

This article was originally published on MedicalXpress.com

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