Dual vector gene therapy trial offers hope for Tay-Sachs and Sandhoff diseases

Patients in a Phase I/II clinical trial conducted by UMass Chan Medical School of a dual vector gene therapy for GM2 gangliosidosis, which includes Tay-Sachs and Sandhoff diseases, exhibited a biochemical correction of the disease with minimal adverse reactions.

This article was originally published on MedicalXpress.com

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